Kalydeco Drug Gets Approval from FDA

KalydecoIt has been reported that drug called Kalydeco has been approved by the US Food and Drug Administration (FDA) for treating cystic fibrosis. The pill thus approved would target the genetic mutation which causes the disease.

Cystic fibrosis is a deadly disease, as it causes the development of unusually thick, sticky mucus in the body of the victim which block the lungs, pancreas and even makes it hard for the enzymes to help body in breaking down the food absorbed by the body.

Those who become a victim of the disease find it hard to breathe. It is believed that the approval of Kalydeco would help 30,000 cystic fibrosis patients in the US and 100,000 patients worldwide to relive from the pain.

If prescribed, patients would be required to take the medicine twice a day. At present, a cystic fibrosis patient is required to wear vibrating vests to dislodge mucus build-up. It has been informed that in the US, about 4% of the cystic fibrosis patients come in contact with the disease because of genetic mutation.

The drug, Kalydeco, would target the mutated genes and thus would prevent the building of mucus. The drug has gone through clinical trial and it is believed to be safe for the usage. However, buying Kalydeco won’t be easy as it is being categorized among the most expensive drugs.

The drug has been produced by the Vertex Pharmaceuticals. The Vertex has said that they would be providing financial aid to the patients. The drug has been allowed to be prescribed to kids of six years old. The Food and Drug Administration is now conducting studies to gauge whether or not the drug could be provided to kids under the age of two.